Dossier
Dr. Haydar Frangoul
Coverage of Dr. Haydar Frangoul in the Nexus archive.
- FDA approves gene therapy for sickle cell disease in children as young as 2 years old
The FDA has approved a gene therapy for sickle cell disease in children as young as 2 years old, expanding access previously limited to those 12 and older. The treatment involves gene-editing a patient's stem cells to produce fetal hemoglobin, offering a potential cure without requiring a donor match.
- ‘A leap of faith’: Nashville teen makes history with gene-editing treatment for sickle cell disease
A 13-year-old Nashville boy, Rickey Buggs, underwent a 42-day gene-editing treatment at TriStar Centennial Children’s Hospital under Dr. Haydar Frangoul, potentially offering a cure for his sickle cell disease. The therapy, described as transformative, marks a significant advancement for patients without family matches for traditional treatments.